through-the-keyhole
28 June 2013Americas

A rare opportunity: aTyr Pharma and orphan drugs

In the US, a rare or orphan disease is defined as a condition that affects fewer than 200,000 Americans. Europe recognises rare diseases as those that affect fewer than one per 2,000 people. While there is no standard for what defines a rare disease, it is agreed that they are often genetic, and usually life-threatening.

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