As support for the study of rare diseases picks up, how does a good IP strategy bring orphan drugs to market? LSIPR spoke to aTyr Pharma’s chief executive John Mendlein to find out.
In the US, a rare or orphan disease is defined as a condition that affects fewer than 200,000 Americans. Europe recognises rare diseases as those that affect fewer than one per 2,000 people. While there is no standard for what defines a rare disease, it is agreed that they are often genetic, and usually life-threatening.
An estimated 6,000 to 8,000 rare diseases, including Huntington’s disease, Crohn’s disease and Duchenne muscular dystrophy, affect 25 million people in the US, and 29 million in the EU.
For many years, patients with rare diseases struggled to get access to treatments, as drug companies could rarely profit from developing drugs for such small populations.
Life Sciences Intellectual Property Review (LSIPR) tracks the increasing challenges for intellectual property specialists in the rapidly evolving world of life sciences. From gene patents to stem cell research, we provide the very best news and analysis.
To continue reading this article and to access 4,500+ articles, our digital magazines and special reports published for LSIPR subscribers only then you will need a subscription.
If you are already subscribed please login.
Official LSIPR subscribers include:
Allen & Overy
Arnold & Siedsma
Birch, Stewart, Kolasch & Birch LLP (BSKB)
Carpmaels & Ransford
European Patent Office
George Washington Law School
Kirkland & Ellis International LLP
Marks & Clerk
NiKang Therapeutics Inc.
Powell Gilbert LLP
Procopio, Cory, Hargreaves & Savitch LLP
The United States Patent and Trademark Office (USPTO)
World Intellectual Property Office
For multi-user price options, or to check if your company has an existing subscription we can add you into for FREE, please contact Atif at firstname.lastname@example.org.
If you have any technical issues please email tech support.
aTyr Pharma, orphan drugs, IP strategy, rare diseases, physiocrines